A new study argues that the prevalence of autism in human populations may reflect an evolutionary trade-off embedded within our genetic heritage. Researchers say that rapid changes in certain brain ...

A gene therapy injected into patients’ brains slowed progression of the disease by 75 percent, preliminary findings reported.

When a key protein regulator dials down DNA repair mechanisms, our cells accumulate more mutations, which may cause us to age faster ...

Junk DNA” may hold the key to treating tough cancers. Existing drugs exploit weaknesses in cells with gene mutations. Researchers at King’s College London have identified a promising strategy for ...

An experimental gene therapy was found to slow the progression of Huntington's disease, marking a major step toward a ...

The clearance of Inluriyo is another development among a group of oral medicines aiming to supplant a widely used, injectable ...

Study in JAMA Oncology: aspirin may cut cancer risk for some adults over 70 and raise it for others. Genetics, smoking, and BMI help guide decisions.

An experimental gene therapy has slowed the progression of Huntington’s disease by 75 percent, according to results reported ...

Drugmaker uniQure reported the results of its small but “groundbreaking” Phase I/II study this week, finding that a high dose ...

Huntington’s disease has been successfully treated for the first time using a gene therapy, which may be available in the US ...

Natural systems such as CRISPR-associated transposons (CASTs) offer a targetable, one-step way to edit genomes. However, ...

For centuries, we’ve thought of these changes as part of the "genetic lottery," something we can't control. Science is now ...