The prize is an oral spleen tyrosine kinase (SYK) inhibitor, called cevidoplenib, which has been developed by Korea’s Oscotec ...

Funding supports research into sickle cell disease, thalassemia, leukemia and other pediatric blood disorders.

Agios obtains exclusive global rights to novel, late-stage, next-generation, oral SYK inhibitorAgreement diversifies Agios’ rare hematology portfolio with expansion into immune thrombocytopenia, ...

The story has additionally reignited ethical debates surrounding the decision to have another child partly to assist with medical treatment for an older sibling. While the issue remains controversial ...

A 15-year-old Chinese girl who has been suffering from a severe blood disorder most of her life is slowly recovering after receiving a transplant from her newborn brother. Xiaoyan from southern ...

When most couples plan a pregnancy, genetics rarely makes the list. Timing, finances, work schedules, these feel immediate and real. Inherited disorders feel distant, something that only affects ...

Kristine Xoing documented her daughter's cancer journey online to help other families ...

Children’s Healthcare of Atlanta, already one of the largest hospital systems in the country, will soon open a state-of-the-art hospital with 446 hospital beds and several acres of lush green space — ...

Physiologically based ferritin thresholds for iron deficiency (ID) onset are consistently higher than current CDC thresholds for children.

A simple urine test may help identify children at risk for autism sooner than current assessments—opening the door for ...

When he was 2-and-a-half, Lucas was diagnosed with neuroblastoma and a rare autoimmune disease caused by the tumor. The ...

For ten years, the Fr1da study, coordinated by Helmholtz Munich, has been investigating whether early stages of type 1 diabetes in children can be detected in routine pediatric care. The latest ...