Columnist Robin Stemple didn't pay much attention to a random bug bite at first, but his situation dramatically worsened.

The FDA has granted orphan drug designation to CRD-003, an investigational gene therapy for limb-girdle muscular dystrophy ...

The U.S. Food and Drug Administration (FDA) has granted orphan drug status to NS-051/NCNP-04, an exon-skipping therapy ...

Adaptive clothing for Duchenne muscular dystrophy offers comfort, ease, and independence for those with muscle weakness and ...

While I was driving, walking, and living independently in high school, he’d had the opposite experience. For Andrew, his high school days consisted of bone breaks, personal care assistants, hospital ...

My name is Patrick, and I’m a 31-year-old man living with Duchenne muscular dystrophy. I live with my parents because I require 24-hour care. I need help with almost everything in my day-to-day life, ...