A gene therapy injected into patients’ brains slowed progression of the disease by 75 percent, preliminary findings reported.

Researchers at the University of Oslo and Oslo University Hospital have developed a promising new immunotherapy targeting the CTNNB1 gene mutation associated with various aggressive cancers like lung ...

When a key protein regulator dials down DNA repair mechanisms, our cells accumulate more mutations, which may cause us to age faster ...

Junk DNA” may hold the key to treating tough cancers. Existing drugs exploit weaknesses in cells with gene mutations. Researchers at King’s College London have identified a promising strategy for ...

An experimental gene therapy was found to slow the progression of Huntington's disease, marking a major step toward a ...

The clearance of Inluriyo is another development among a group of oral medicines aiming to supplant a widely used, injectable ...

Study in JAMA Oncology: aspirin may cut cancer risk for some adults over 70 and raise it for others. Genetics, smoking, and BMI help guide decisions.

For decades, scientists have known that bacteria can exchange genetic material, in a process called horizontal gene transfer.

An experimental gene therapy has slowed the progression of Huntington’s disease by 75 percent, according to results reported by the biotechnology company uniQure this week.

Scientists developed a new nanostructure that triples CRISPR’s ability to enter cells, unlocking even more power to treat ...

Drugmaker uniQure reported the results of its small but “groundbreaking” Phase I/II study this week, finding that a high dose ...

Huntington’s disease has been successfully treated for the first time using a gene therapy, which may be available in the US ...