Adaptive clothing for Duchenne muscular dystrophy offers comfort, ease, and independence for those with muscle weakness and ...

The FDA has granted orphan drug designation to CRD-003, an investigational gene therapy for limb-girdle muscular dystrophy ...

Columnist Robin Stemple didn't pay much attention to a random bug bite at first, but his situation dramatically worsened.

The U.S. Food and Drug Administration (FDA) has granted orphan drug status to NS-051/NCNP-04, an exon-skipping therapy ...

Columnist Patrick Moeschen shares what he wishes doctors understood about treating patients with rare diseases such as ...

One thing I love about living in the Midwest is enjoying all four seasons. The last week of summer is nearly over, and autumn officially begins next week. On a walk yesterday, I noticed the first ...

Patients aged 10-50 are being sought for a clinical trial testing SAR446268, a gene therapy for myotonic dystrophy type 1 (DM1).

Living with Duchenne muscular dystrophy means every trip to the hospital is key to my survival. From heart scans to routine medical appointments, leaving home is never simple. I rely on my mom to ...

I was diagnosed with Duchenne muscular dystrophy at age 3. By the time I was 10, I was exclusively using a power wheelchair for mobility — and I’ve been rolling ever since. Living with a chronic ...

A combined regimen of testosterone and growth hormone improves muscle mass, strength, and mobility in men with FSHD, a study ...

Mallory Dupree hasn't let a Duchenne muscular dystrophy diagnosis keep her from living the life she wants to live.

Mallory Dupree lives with Duchenne muscular dystrophy and whose experience in Duchenne advocacy began as a teen, meeting with members of Congress to advocate for the passage of the MD-CARE Act. Since ...